Amicus Therapeutics

Amicus Therapeutics Announces Approval and Launch of New Pompe Disease Therapy in the European Union

PHILADELPHIA, PA — Amicus Therapeutics (Nasdaq: FOLD) announced that the European Commission (EC) has granted approval for Opfolda® (miglustat) 65mg capsules, an enzyme stabilizer of cipaglucosidase alfa, a long-term enzyme replacement …

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INOVIO Pharmaceuticals

European Committee Provides Positive Opinion on INOVIO’s Application for Orphan Drug Designation for INO-3107

PLYMOUTH MEETING, PA — INOVIO (NASDAQ: INO) announced that the European Committee for Orphan Medicinal Products (COMP) recently provided a positive opinion on INOVIO’s application for orphan drug designation in …

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